RI USH SIG Winter Newsletter

On December 2nd Retina International sent the RI USH SIG Winter Newsletter We are happy to send you the RI USH SIG Winter Newsletter providing you with an update of the latest and upcoming news relevant for people living with Usher Syndrome and with a resource file on USH subtypes, genetic testing and USH genes.
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ProQR Doses First Patient in Phase 1/2 STELLAR Trial of QR-421a for Usher Syndrome Type 2

Original text here LEIDEN, Netherlands and CAMBRIDGE, Mass., March 11, 2019 (GLOBE NEWSWIRE) — ProQR Therapeutics N.V. (Nasdaq:PRQR), a company dedicated to changing lives through the creation of transformative RNA medicines for the treatment of severe genetic rare diseases, today announced the first patient dosed in the Phase 1/2 STELLAR clinical trial for QR-421a in patients with Usher syndrome type 2 or non-syndromic retinitis pigmentosa (RP).
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International Symposium on Usher Syndrome 2018

Last week the International Symposium on Usher Syndrome was held in Mainz. It was a 3-day event, we only attended the patient’s symposium as I was afraid that the 2 scientific days would be too complicated to follow anyway (and I would be braindead before the patient program even started…).
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