USH2A Clinical Trial Webinar, presented by ProQR

The content in this page is take from the Usher Syndrome Coalition website and it is of their property. We are authorized to reproduce this content on our website) February 7, 2022: ProQR and the Usher Syndrome Coalition hosted a webinar about the newly announced clinical trials, “Sirius” and “Celeste,” for individuals with Usher syndrome type 2A (USH2A).
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QR-421a: Showing Benefits on One out of Four Usher Syndrome patients

Original article on AP News QR-421a showed early and encouraging evidence of activity, with 25% of patients showing a benefit across multiple concordant outcome measures and was well tolerated with no serious adverse events — QR-421a is the second ophthalmology program where clinical activity was predicted by translational models, further validating the platform — COVID-19 pandemic expected to impact timelines for the pipeline — ProQR anticipates its cash runway will fund operations into H2 2022 LEIDEN, Netherlands & CAMBRIDGE, Mass.,
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