ProQR Announces Positive Results from Clinical Trial of QR-421a in Usher Syndrome

Orignal Post here ProQR Announces Positive Results from Clinical Trial of QR-421a in Usher Syndrome and Plans to Start Pivotal Trials QR-421a demonstrated a concordant benefit in multiple measures of vision, including best corrected visual activity (BCVA), static perimetry, and retinal imaging (OCT) QR-421a observed to be well tolerated with no serious adverse events reported Two pivotal Phase 2/3 trials are expected to start by the end of 2021 Management to host a conference call today at 8:15am EDT LEIDEN, Netherlands & CAMBRIDGE, Mass.,
Read

Usher Syndrome Community

It is important to create an Usher Syndrome Community because we need to join efforts, resources and ideas and address them in one direction to have a stronger impact.
Read

The Visual Bucket List Foundation

Do you remember the story of Lizzy? She is the little girl from Ohio with Usher Syndrome that in 2016 was all over the news because she was able to meet Pope Francis, as one of her Bucket List wishes.