RI USH SIG – Spring Newsletter

Retina International Usher Syndrome Special Interest Group Spring Newsletter – Update on events & news relevant during the COVID-19 pandemic RI USH SIG Dominique Sturz (AT), Melissa Chaikof (US), Carol Brill (IRL), Dario Sorgato (IT) We hope that you are all fine and healthy despite the COVID-19 pandemic.
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QR-421a: Showing Benefits on One out of Four Usher Syndrome patients

Original article on AP News QR-421a showed early and encouraging evidence of activity, with 25% of patients showing a benefit across multiple concordant outcome measures and was well tolerated with no serious adverse events — QR-421a is the second ophthalmology program where clinical activity was predicted by translational models, further validating the platform — COVID-19 pandemic expected to impact timelines for the pipeline — ProQR anticipates its cash runway will fund operations into H2 2022 LEIDEN, Netherlands & CAMBRIDGE, Mass.,
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