USH2A Clinical Trial Webinar, presented by ProQR

The content in this page is take from the Usher Syndrome Coalition website and it is of their property. We are authorized to reproduce this content on our website) February 7, 2022: ProQR and the Usher Syndrome Coalition hosted a webinar about the newly announced clinical trials, “Sirius” and “Celeste,” for individuals with Usher syndrome type 2A (USH2A).
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ProQR Announces Positive Results from Clinical Trial of QR-421a in Usher Syndrome

Orignal Post here ProQR Announces Positive Results from Clinical Trial of QR-421a in Usher Syndrome and Plans to Start Pivotal Trials QR-421a demonstrated a concordant benefit in multiple measures of vision, including best corrected visual activity (BCVA), static perimetry, and retinal imaging (OCT) QR-421a observed to be well tolerated with no serious adverse events reported Two pivotal Phase 2/3 trials are expected to start by the end of 2021 Management to host a conference call today at 8:15am EDT LEIDEN, Netherlands & CAMBRIDGE, Mass.,
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RI USH SIG – Spring Newsletter

Retina International Usher Syndrome Special Interest Group Spring Newsletter – Update on events & news relevant during the COVID-19 pandemic RI USH SIG Dominique Sturz (AT), Melissa Chaikof (US), Carol Brill (IRL), Dario Sorgato (IT) We hope that you are all fine and healthy despite the COVID-19 pandemic.
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QR-421a: Showing Benefits on One out of Four Usher Syndrome patients

Original article on AP News QR-421a showed early and encouraging evidence of activity, with 25% of patients showing a benefit across multiple concordant outcome measures and was well tolerated with no serious adverse events — QR-421a is the second ophthalmology program where clinical activity was predicted by translational models, further validating the platform — COVID-19 pandemic expected to impact timelines for the pipeline — ProQR anticipates its cash runway will fund operations into H2 2022 LEIDEN, Netherlands & CAMBRIDGE, Mass.,
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RI USH SIG Winter Newsletter

On December 2nd Retina International sent the RI USH SIG Winter Newsletter We are happy to send you the RI USH SIG Winter Newsletter providing you with an update of the latest and upcoming news relevant for people living with Usher Syndrome and with a resource file on USH subtypes, genetic testing and USH genes.
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